Tag Archives: Disease

With Gamifant launch rolling, Sobi unveils more data backing the rare disease med

SAN DIEGO—Armed with last month’s FDA approval, Sobi is rolling out its newly minted rare disease drug Gamifant with a small, targeted sales force, and Monday it unveiled more of the data that won the agency’s favor in the first place. In a phase 2/3 trial of Gamifant in primary haemophagocytic lymphohistiocytosis (HLH), 64.7% of… Read More »

How A Hematologist Can Use IVF To Treat And Prevent Disease, Lower Costs And Make CRISPR Irrelevant

As the annual meeting of the American Society of Hematology takes place this week in San Diego, I humbly offer a plan to treat current patients with hemophilia, sickle cell anemia, thalassemia and other genetic hematologic diseases AND prevent future cases AND lower healthcare costs AND remove the incentives to alter the DNA inside embryos… Read More »

Vitamin D and Fish Oils Are Ineffective for Preventing Cancer and Heart Disease

In recent years, many Americans have embraced vitamin D and fish oil pills, their enthusiasm fueled by a steady trickle of suggestive research studies linking higher levels of vitamin D with lower rates of cancer and other ills, and fish consumption with reduced heart disease. Now a large and rigorous government-funded randomized trial — the… Read More »