Tag Archives: ‘rare’

With Gamifant launch rolling, Sobi unveils more data backing the rare disease med

SAN DIEGO—Armed with last month’s FDA approval, Sobi is rolling out its newly minted rare disease drug Gamifant with a small, targeted sales force, and Monday it unveiled more of the data that won the agency’s favor in the first place. In a phase 2/3 trial of Gamifant in primary haemophagocytic lymphohistiocytosis (HLH), 64.7% of… Read More »

FDA warns against honey pacifiers after Texas infants hospitalized with ‘rare’ illness

[unable to retrieve full-text content]Parents, be warned: The U.S. Food and Drug Administration (FDA) is cautioning caregivers to not give honey to babies under one year of age, as four infants in Texas were recently hospitalized after using pacifiers that contained the sweet substance. FOX News